Posts Tagged ‘BioMarin’
Taking a shot: An orphan drug trial that drew an international crowd of patients nears its end
When Sarah Morrell was first diagnosed with Morquio syndrome, a rare, incurable disease that crippled her joints and deformed her vertebrae, her family never expected the illness would cause her to travel halfway around the world to have an experimental treatment made from Chinese hamster ovaries injected into her veins.
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